Restoration of exocrine pancreatic function in older children with cystic fibrosis on ivacaftor - 24/08/20
Abstract |
Prior to the use of cystic fibrosis (CF) modulator therapy, exocrine pancreatic insufficiency in CF was thought to be irreversible. Improvement in pancreatic function on ivacaftor has been reported in open label studies in 1–5 year olds. The mechanism by which ivacaftor might improve exocrine pancreatic function is unclear. Although the effect of ivacaftor on pancreatic function may be more significant in younger children, evidence is mounting that there may still be potential for improvement in older children on long term therapy.
Le texte complet de cet article est disponible en PDF.Keywords : Pancreatic function, Cystic fibrosis, Ivacaftor, CFTR modulator
Vol 35
P. 99-102 - septembre 2020 Retour au numéroBienvenue sur EM-consulte, la référence des professionnels de santé.
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